Paroxysmal nocturnal hemoglobinuria
Related or unrelated donor transplant indications
- ≤ 60 years old for related or unrelated donor transplant, AND
- Severe disease defined as one of the following characteristics:
- An episode of severe thrombosis
- Severe aplastic anemia (the patient must have failed ATG if the donor is unrelated or if the patient is older than 40)
- Transformation into a myelodysplastic syndrome
